April 26, 2024

New Way To Develop Drugs Without Side Effects – To Treat Obesity, Pain, Osteoporosis, and Neurological Disorders

GPCR is like a snake with seven sections traversing in and out of the cookie sandwich surface area if the cell membrane is like an Oreo cookie sandwich. The extracellular loops are the inbox for messages. When a message particle binds to the extracellular side of the receptor, it activates a shape change activating G proteins and ß-arrestin protein connected to the intracellular side of the receptor. Like a molecular relay, the info passes downstream and affects numerous bodily processes. That is how we see, smell, and taste, which are feelings of light, taste, and odor messages.
An artists impression of resulting targeted response from GPCR activation from inside the cell. Credit: Kobayashi and Kawakami et al., 2023
Adverse adverse effects take place if drugs acting upon GPCRs trigger several signaling pathways rather than a particular target path. That is why drug development concentrates on triggering particular molecular signal pathways within cells. Triggering the GPCR from inside the cell instead of outside the cell could be one method to attain uniqueness. But previously, there was no proof of direct activation of only the intracellular side of GPCRs without the initiations from the extracellular side.
A group of scientists headed by Osamu Nureki, a professor at the University of Tokyo, and his lab, discovered a new receptor activation mode of a bone metabolism-related GPCR called human parathyroid hormone type 1 receptor (PTH1R) without signal transduction from the extracellular side.
” Understanding the molecular mechanism will enable us to design ideal drugs,” says Kazuhiro Kobayashi, a doctoral trainee and an author of the research study. Such a drug uses “an appealing treatment for osteoporosis.”
Kobayashi has actually been performing research study on bone formation in animal designs given that he was an undergrad. “Treatments for osteoporosis that target PTH1R require strict dose, have administration route constraints, and there arent yet any much better options,” he says. That motivated their team to look for much better drug design methods targeting the parathyroid hormonal agent receptor.
To understand function through structure, they utilized cryo-electron microscopy and exposed the 3D structure of the PTH1R and G protein bound to a message molecule. The team synthesized a non-peptide message molecule called PCO371 which binds to the intracellular region of the receptor and interacts directly with G protein subunits. In other words, PCO371 triggers the receptor after going into the cell.
The PCO371-bound PTH1R structure can straight and stably regulate the intracellular side of PTH1R. And due to the fact that PCO371 triggers only G protein and not ß-arrestin it does not cause adverse effects. This specificity of its binding and receptor activation mode makes it an appropriate prospect for prospective small-molecule-based drugs for class B1 GPCRs, like PTH1R, which currently lack oral administrative drug ligands. Such drugs would have decreased unfavorable results and concerns on patients as they act upon particular molecular paths.
The findings from this study will assist “establish brand-new drugs for disorders such as obesity, discomfort, osteoporosis, and neurological disorders.”
The research study appears in the journal Nature.
Recommendation: “Class B1 GPCR activation by an intracellular agonist” by Kazuhiro Kobayashi, Kouki Kawakami, Tsukasa Kusakizako, Atsuhiro Tomita, Michihiro Nishimura, Kazuhiro Sawada, Hiroyuki H. Okamoto, Suzune Hiratsuka, Gaku Nakamura, Riku Kuwabara, Hiroshi Noda, Hiroyasu Muramatsu, Masaru Shimizu, Tomohiko Taguchi, Asuka Inoue, Takeshi Murata and Osamu Nureki, 7 June 2023, Nature.DOI: 10.1038/ s41586-023-06169-3.

An artists impression of the GPCR activation from inside the cell. Credit: Kobayashi and Kawakami et al., 2023
Researchers discovered an unique technique to trigger G-protein combined receptors from inside the cells, and it helps establish drugs without negative effects.
The group recognized a particle, PCO371, that communicates with the intracellular area of a specific GPCR, using an appealing method for treating conditions like weight problems, pain, osteoporosis, and neurological conditions.
If a drug particle or a ligand is a message, an inbox is normally a receptor in the cell membrane. One such receptor included in communicating molecular signals is a G protein-coupled receptor (GPCR). Japanese researchers now reveal a new way of activating GPCR by activating shape modifications in the intracellular region of the receptor.

One such receptor included in relaying molecular signals is a G protein-coupled receptor (GPCR). Japanese researchers now expose a new method of triggering GPCR by setting off shape changes in the intracellular area of the receptor. Adverse side impacts ensue if drugs acting on GPCRs trigger multiple signaling pathways rather than a particular target pathway. Triggering the GPCR from inside the cell rather than outside the cell could be one way to accomplish uniqueness. This uniqueness of its binding and receptor activation mode makes it a suitable prospect for potential small-molecule-based drugs for class B1 GPCRs, like PTH1R, which currently do not have oral administrative drug ligands.